Dr Niranjan Rathod, Associate Director and HOD, Haemato – Oncology and Bone Marrow Transplant, Nanavati Hospital, maintains that gene therapy could herald a revolutionary shift in treatment of thalassemia, but research is still at a nascent stage.
What is gene therapy, with reference to thalassemia?
Gene therapy for thalassemia involves genetic manipulation of the defective gene responsible for thalassemia, in patient derived stem cells with the help of a virus vector to correct the…